mirdametinib Archives - Children's Tumor Foundation

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Featured Featured EU Science & Research

CTF CEO Annette Bakker Moderates Panel at World Orphan Drug Congress 2025

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CTF in the News Featured Featured EU Science & Research

How a Once-Abandoned Drug Found New Life – and Changed the Future for NF Patients

Child cheering beside text: "IT'S A GO! FDA approves drug for children and adults with NF1." Website: ctf.org.

NF1 Pharma Science & Research Top Story Top Story EU

IT’S A GO! NF’s NEXT BIG WIN!

A woman with a facial difference, wearing a pink floral shirt, is in front of a blue background with "give" and "Children’s Tumor Foundation" text and a heart symbol.

Featured NF1 Pharma Story of NF Video

Give for Tomorrow: Marcia’s Story and the Promise of More Treatments