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Johns Hopkins Researcher Seeking Participants for Study on Bullying and Cyberbullying

Nov 26, 2018, Posted in Outside Opportunities, NF1, Science

Genetic counselers at the Johns Hopkins Comprehensive Neurofibromatosis Center are conducting a survey to better understand how bullying and cyberbullying are impacting their adolescent NF patients. This research will be used to better inform their own practice, as well as to develop resources that will be available to teens, families and health care providers of those with NF1.

Call for Applications for the class of 2019 Francis S. Collins Scholars

Nov 7, 2018, Posted in Outside Opportunities, NF1, Science

The Neurofibromatosis Therapeutic Acceleration Program (NTAP) is now accepting applications for the Francis S. Collins Scholars Program in Neurofibromatosis Clinical and Translational Research. The Collins Scholars program brings together a community of exceptionally well-trained clinician scientists who will be leaders in the field of NF1 research.

Workshop Recap: The Promise of Gene Therapy Approaches to Rare Diseases

Sep 27, 2018, Posted in Science

WORKSHOP RECAP: The Growing Promise of Gene Therapy Approaches to Rare Diseases

On Aug 20-21, 2018 the National Center for Advancing Translational Sciences (NCATS) and FDA’s Center for Biologics Evaluation and Research (CBER) hosted a workshop on gene therapy in Bethesda, MD. Titled ‘The Growing Promise of Gene Therapy Approaches to Rare Diseases,’ the workshop was attended by experts from academia and industry, NIH and FDA staff, representatives from several rare disease foundations, and other stakeholders. The two-day event was filled with presentations and panel discussions on advancements and challenges in preclinical and clinical development of gene therapy products, vector manufacturing processes, public-private partnerships including with research foundations, business models, patient access especially in very low prevalence diseases, and reimbursement models.

2019 Pershing Square Sohn Cancer Research Prize is Opening for Applications

Sep 16, 2018, Posted in Awards, Science

The Pershing Square Sohn Cancer Research Alliance (PSSCRA) will open for applications for its 2019 Pershing Square Sohn Prize for Young Investigators in Cancer Research on October 1st, 2018. At least six New York City-area-based scientists will each be awarded $200,000/year – for up to three years – to empower them to pursue groundbreaking research.

NF1 Gene Therapy Initiative: Request for Applications

Sep 11, 2018, Posted in Awards, NF1, Science

The Children’s Tumor Foundation (CTF) is pleased to announce the initiation of a research program in gene-based therapeutic approaches for the treatment of neurofibromatosis type 1 (NF1). This initiative begins through this request for applications (RFA), with the first goal to fund two proof-of-principle studies in NF1 gene editing. Funding for each study will be $240,000 total (inclusive of 10% indirect costs) for a duration of two years.